Pipeline Build | iECURE

Therapeutic area

Discovery

Preclinical

Phase 1

Phase 2

Phase 3

Knock-in Programs

Dual AAV with ARCUS Nuclease

OTC

Citrullinemia Type 1

PKU

Preclinical

Discovery

Discovery

LNP/Nuclease/AAV

Multiple programs under evaluation

Discovery

Partnered Program

FH

PCSK9-Knockout

Preclinical